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A Rare Lysosomal Storage Disease
Contact: info@npcfund.org

Posts Tagged ‘Nuerological’

FDA says Hold Off on Zavesca (Miglustat) approval.

On March 9, 2010 the FDA has requested additional preclinical and clinical information regarding Zavesca (Miglustat) before giving the ultimate approval that the Niemann-Pick Type C community was hoping for.

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