A Rare Lysosomal Storage Disease

Archive for September 2010

Impact of Niemann-Pick Type C

Actelion Pharmaceuticals LTD produced a short video on two families and how Niemann-Pick Type C Disease has impacted their lives. Hollie Carter and Annie Pyne are featured in this video. They both are youngsters living with this disease. At first sight we all instantly start to evaluate […]

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Your Vote Can Save Lives | Rare Disease

Please watch this short message! Just hit the right arrow to proceed through! Your vote could help us win! We want to do something special with this money!

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