A Rare Lysosomal Storage Disease

Archive for February 2010

Social Security Adds 38 New Medical Conditions that Qualify for Disability

Social Security adds 38 new medical conditions that qualify for disability help.  The new conditions range from early-onset Alzheimer’s disease to rare diseases that primarily affect children which includes Niemann-Pick Type C! Personally this seems like a relief for so many families. One of the goals of […]

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UPDATE 2-US FDA panel backs new use for Actelion drug [Zavesca]

We’re a few weeks behind in updating this information but some big steps have happened recently regarding the potential FDA approval for Zavesca. The US Advisory panel on Jan. 12th recommended approval! This snippet is from the article on Reuters regarding the breaking news: Doctors can prescribe […]

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