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A Rare Lysosomal Storage Disease
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Posts Tagged ‘Miglustat’

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10 Apr 2010

Canada Receives First Approved Treatment For Niemann-Pick Type C

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Written by , Posted in Blog, News, Zavesca (Miglustat) | 1 Comment

Canada has a lot to celebrate for their current and future patients living with the “Childhood Alzheimer’s” or Niemann-Pick Type C (NPC). During the last full week of March 2010, the announcement came down that Health Canada [The Food Directorate, the Therapeutic Products Directorate and the Natural […]

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21 Nov 2009

New therapies – Niemann-Pick type C disease

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Written by , Posted in Blog, News, Therapies, What is NPC | Leave a comment

Abstract: Niemann-Pick disease type C (NP-C) is an autosomal recessive disorder characterized by progressive neurological deterioration leading to premature death.

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