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A Rare Lysosomal Storage Disease
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Posts Tagged ‘Cyclodextrins’

Orphan Drug Designation for Cyclodextrin | NPC

This week the FDA has stated formally that they see promise in the use of Cyclodextrin in treating Niemann-Pick Type C (NPC) by granting its “Orphan Drug Designation”. In January of 1983, the Orphan Drug Act (ODA) was passed into law in the United States with consistent […]

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